Viewing Study NCT02376751

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Ignite Creation Date: 2025-12-24 @ 11:55 PM
Ignite Modification Date: 2026-03-01 @ 1:45 PM
Study NCT ID: NCT02376751
Status: NO_LONGER_AVAILABLE
Last Update Posted: 2016-06-08
First Post: 2015-02-25
Is NOT Gene Therapy: True
Has Adverse Events: False
Brief Title: An Expanded Access Protocol for Sebelipase Alfa for Patients With Lysosomal Acid Lipase Deficiency
Sponsor: Alexion Pharmaceuticals, Inc.
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Lysosomal Acid Lipase Deficiency View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Cholesteryl Ester Storage Disease View
None Acid lipase disease View
None Cholesterol ester hydrolase deficiency View
None LIPA Deficiency View
None Wolman disease View
None Lysosomal Storage Disease View