Viewing Study NCT04601051

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Ignite Creation Date: 2025-12-24 @ 11:55 PM
Ignite Modification Date: 2026-02-01 @ 10:23 PM
Study NCT ID: NCT04601051
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-05-01
First Post: 2020-10-19
Is NOT Gene Therapy: True
Has Adverse Events: False
Brief Title: Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NTLA-2001 in Patients With Hereditary Transthyretin Amyloidosis With Polyneuropathy (ATTRv-PN) and Patients With Transthyretin Amyloidosis-Related Cardiomyopathy (ATTR-CM)
Sponsor: Intellia Therapeutics
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Transthyretin-Related (ATTR) Familial Amyloid Polyneuropathy View
None Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy View
None Wild-Type Transthyretin Cardiac Amyloidosis View
Keywords:

Keywords

Keyword Brief Keyword Text View
None NTLA-2001 View
None Pharmacokinetics View
None Pharmacodynamics View
None Neurologic Function View
None Clustered Regularly Interspaced Short Palindromic Repeats View
None CRISPR View
None Polyneuropathy View
None ATTR View
None Transthyretin View
None TTR View
None Amyloidosis View
None Familial Amyloid Polyneuropathy View
None FAP View
None Cardiomyopathy View