Viewing Study NCT04221451


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Study NCT ID: NCT04221451
Status: TERMINATED
Last Update Posted: 2024-12-30
First Post: 2020-01-06
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Multinational, Randomized, Double-blind, Placebo-controlled Study to Assess the Efficacy, Pharmacodynamics, Pharmacokinetics, and Safety of Venglustat in Late-onset GM2
Sponsor: Genzyme, a Sanofi Company
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Tay-Sachs Disease View
None Sandhoff Disease View
Keywords: