Viewing Study NCT06283212


Ignite Creation Date: 2025-12-26 @ 10:44 PM
Ignite Modification Date: 2025-12-30 @ 11:05 PM
Study NCT ID: NCT06283212
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-12-12
First Post: 2024-02-22
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Clinical Study to Evaluate the Safety and Efficacy of ETX101, an AAV9-Delivered Gene Therapy in Children With SCN1A-positive Dravet Syndrome
Sponsor: Encoded Therapeutics
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Dravet Syndrome View
Keywords: