Viewing Study NCT04925206


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Ignite Modification Date: 2026-02-02 @ 6:38 AM
Study NCT ID: NCT04925206
Status: TERMINATED
Last Update Posted: 2025-03-30
First Post: 2021-06-04
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: A Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia
Sponsor: EdiGene (GuangZhou) Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Transfusion Dependent Beta-Thalassaemia View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Beta-Thalassaemia View
None CRISPR-Cas9 View
None Human Hematopoietic Stem and Progenitor Cells View