Viewing Study NCT07285369

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Ignite Creation Date: 2025-12-24 @ 11:03 PM
Ignite Modification Date: 2026-03-08 @ 1:58 AM
Study NCT ID: NCT07285369
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-12-16
First Post: 2025-11-21
Is NOT Gene Therapy: True
Has Adverse Events: False
Brief Title: High-Dose Ambroxol in Pediatric Type III Gaucher Disease (GD3)
Sponsor: Agyany Pharma LTD
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Gaucher Disease, Type 3 View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Type III Gaucher Disease View
None Gaucher Disease View
None GD3 View
None Ambroxol View
None Pharmacologic chaperone View
None Ataxia View
None Myoclonus View
None Neurological manifestations View
None Lysosomal storage disorder View