Viewing Study NCT05027269


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Ignite Modification Date: 2026-02-25 @ 4:57 PM
Study NCT ID: NCT05027269
Status: COMPLETED
Last Update Posted: 2024-02-05
First Post: 2021-08-24
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Study of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients
Sponsor: Avidity Biosciences, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None DM1 View
None Myotonic Dystrophy 1 View
None Myotonic Dystrophy View
None Myotonic Dystrophy Type 1 (DM1) View
None Dystrophy Myotonic View
None Myotonic Disorders View
None Steinert Disease View
None Myotonic Muscular Dystrophy View
Keywords:

Keywords

Keyword Brief Keyword Text View
None DM1 View
None Myotonic Dystrophy 1 View
None Myotonic Dystrophy Type 1 (DM1) View
None Myotonic Dystrophy View
None DM View
None Dystrophy Myotonic View
None Myotonic Disorders View
None Steinert Disease View
None MARINA View
None Avidity Biosciences View
None Avidity View
None AOC 1001 View
None Myotonic Muscular Dystrophy View