Viewing Study NCT04364269


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Study NCT ID: NCT04364269
Status: COMPLETED
Last Update Posted: 2023-12-14
First Post: 2020-04-01
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: Safety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-thalassaemia
Sponsor: Vifor (International) Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Beta-Thalassemia View
None Non-transfusion-dependent Thalassemia View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Beta-Thalassemia View