Viewing Study NCT00439569


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Study NCT ID: NCT00439569
Status: TERMINATED
Last Update Posted: 2010-09-08
First Post: 2007-02-21
Is NOT Gene Therapy: True
Has Adverse Events: True

Brief Title: Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III
Sponsor: Westat
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Spinal Muscular Atrophy Type II View
None Spinal Muscular Atrophy Type III View
Keywords:

Keywords

Keyword Brief Keyword Text View
None spinal muscular atrophy type II/III View
None SMA type II/III View
None spinal muscular atrophy View
None SMA View
None sodium phenylbutyrate View
None motor neuron disease View
None neuromuscular View
None survival motor neuron View
None SMN View
None dose escalation View