| Keyword Brief | Keyword Text | View |
|---|---|---|
| None | spinal muscular atrophy type II/III | View |
| None | SMA type II/III | View |
| None | spinal muscular atrophy | View |
| None | SMA | View |
| None | sodium phenylbutyrate | View |
| None | motor neuron disease | View |
| None | neuromuscular | View |
| None | survival motor neuron | View |
| None | SMN | View |
| None | dose escalation | View |