Viewing StudyNCT00787995



Ignite Creation Date: 2024-05-05 @ 8:01 PM
Last Modification Date: 2024-10-26 @ 9:57 AM
Study NCT ID: NCT00787995
Status: TERMINATED
Last Update Posted: 2014-12-08
First Post: 2008-11-06

Brief Title: A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA Morquio Syndrome
Sponsor: BioMarin Pharmaceutical
Organization: BioMarin Pharmaceutical

Conditions & Keywords Data

Conditions:
Name
Morquio A Syndrome
MPS IV A
Mucopolysaccharidosis IVA
Keywords:
Name View
ERT View
Mucopolysaccharidosis IV type A View
MPS IV Type A View
Mucopolysaccharidosis IVA View
MPS IVA View
Morquio A Syndrome View
Lysosomal Storage Disorder View
LSD View
N-acetylgalactosamine-6-sulfatase View
galactose-6-sulfatase View
GALNS View
enzyme replacement therapy View