Viewing Study NCT03765632


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Study NCT ID: NCT03765632
Status: COMPLETED
Last Update Posted: 2023-02-01
First Post: 2018-08-08
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID
Sponsor: Great Ormond Street Hospital for Children NHS Foundation Trust
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Severe Combined Immunodeficiency Due to ADA Deficiency View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Gene therapy View
None Hematopoietic stem and progenitor cells View
None Lentiviral vector View
None ADA-SCID View