Ignite Creation Date:
2025-12-24 @ 1:17 PM
Ignite Modification Date:
2026-01-31 @ 5:56 AM
Study NCT ID:
NCT05356195
Status:
RECRUITING
Last Update Posted:
2025-10-14
First Post:
2022-04-07
Is Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia (TDT)
Sponsor:
Vertex Pharmaceuticals Incorporated
Organization: