Viewing Study NCT06475404


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Ignite Modification Date: 2026-01-06 @ 2:04 PM
Study NCT ID: NCT06475404
Status: COMPLETED
Last Update Posted: 2024-07-03
First Post: 2024-06-20
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: A Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy Volunteers
Sponsor: AO GENERIUM
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Mucopolysaccharidosis Type II View
None Metabolic Diseases View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Mucopolysaccharidosis type II View
None Mucopolysaccharidoses View
None Metabolic Diseases View
None Lysosomal Storage Diseases View
None Carbohydrate Metabolism View
None Inborn View
None Metabolism View
None Genetic Diseases View
None Neurobehavioral Manifestations View
None Neurologic Manifestations View
None Genetic Diseases, X-Linked View