Ignite Creation Date:
2025-12-24 @ 7:49 PM
Ignite Modification Date:
2026-03-12 @ 10:20 AM
Study NCT ID:
NCT06149403
Status:
ACTIVE_NOT_RECRUITING
Last Update Posted:
2025-12-22
First Post:
2023-11-17
Is NOT Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
A Study to Investigate the Efficacy and Safety of OTL-203 in Subjects With MPS-IH Compared With Standard of Care With Allogeneic HSCT
Sponsor:
Orchard Therapeutics
Organization:
Conditions & Keywords Data
Conditions:
Conditions
| Condition Brief | Condition Text | View |
|---|---|---|
| None | MPS-IH (Hurler Syndrome) | View |
Keywords:
Keywords
| Keyword Brief | Keyword Text | View |
|---|---|---|
| None | MPS-IH | View |
| None | Hurler | View |
| None | MPS-I | View |
| None | Mucopolysaccharidoses | View |
| None | Mucopolysaccharidosis type I | View |
| None | Hurler syndrome | View |
| None | Mucopolysaccharidosis IH | View |
| None | Gene Therapy | View |
| None | Transplantation | View |
| None | Autologous Lentiviral vector | View |