Viewing Study NCT01858103

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Ignite Creation Date: 2025-12-24 @ 7:48 PM
Ignite Modification Date: 2026-03-11 @ 5:02 PM
Study NCT ID: NCT01858103
Status: APPROVED_FOR_MARKETING
Last Update Posted: 2014-04-02
First Post: 2013-05-15
Is NOT Gene Therapy: True
Has Adverse Events: False
Brief Title: BMN 110 US Expanded Access Program
Sponsor: BioMarin Pharmaceutical
Organization:
Overview Dates Organization Conditions Design Enrollment Locations Outcomes Modules Raw JSON

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Mucopolysaccharidosis IVA View
None Morquio A Syndrome View
None MPS IVA View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Mucopolysaccharidosis IVA Type A View
None MPS IVA Type A View
None Mucopolysaccharidosis IVA View
None MPS IVA View
None Morquio A Syndrome View
None Lysosomal Storage Disorder View
None LSD View
None N-acetylgalactosamine-6-sulfatase View
None N-acetylgalactosamine-6-sulfate View