Viewing StudyNCT06369974



Ignite Creation Date: 2024-05-06 @ 8:23 PM
Last Modification Date: 2024-10-26 @ 3:27 PM
Study NCT ID: NCT06369974
Status: NOT_YET_RECRUITING
Last Update Posted: 2024-04-18
First Post: 2024-03-11

Brief Title: Single Participant Study of an Experimental ASO Treatment for TUBB4A-related Leukodystrophy
Sponsor: Massachusetts General Hospital
Organization: Massachusetts General Hospital

Conditions & Keywords Data

Conditions:
Name
Genetic Disease
Keywords:
Name View
leukodystrophy View
antisense oligonucleotide View
TUBB4A-related leukodystrophy View
Hypomyelination View
ASO View