Viewing StudyNCT06351592



Ignite Creation Date: 2024-05-06 @ 8:22 PM
Last Modification Date: 2024-10-26 @ 3:26 PM
Study NCT ID: NCT06351592
Status: RECRUITING
Last Update Posted: 2024-04-08
First Post: 2024-04-02

Brief Title: First in Human FIH Study of ALN-SOD in Adult Participants With Amyotrophic Lateral Sclerosis Associated With Mutation in the SOD1 Gene SOD1-ALS
Sponsor: Regeneron Pharmaceuticals
Organization: Regeneron Pharmaceuticals

Conditions & Keywords Data

Conditions:
Name
Mutation in the Superoxide Dismutase-1 SOD1 Gene
Amyotrophic Lateral Sclerosis ALS
Keywords:
Name View
symptomatic View
known pathogenic mutation View
predicted pathogenic mutation View