Viewing StudyNCT06100276



Ignite Creation Date: 2024-05-06 @ 7:42 PM
Last Modification Date: 2024-10-26 @ 3:11 PM
Study NCT ID: NCT06100276
Status: RECRUITING
Last Update Posted: 2024-07-09
First Post: 2023-10-20

Brief Title: Safety Tolerability and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants with SOD1 Amyotrophic Lateral Sclerosis SOD1-ALS
Sponsor: UniQure Biopharma BV
Organization: UniQure Biopharma BV

Conditions & Keywords Data

Conditions:
Name
Amyotrophic Lateral Sclerosis
Keywords:
Name View
SOD1 View
Gene Therapy View
AAV adeno-associated virus View
ALS View