Viewing Study NCT04159103


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Study NCT ID: NCT04159103
Status: RECRUITING
Last Update Posted: 2025-10-31
First Post: 2019-11-07
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Open-Label Study of mRNA-3927 in Participants With Propionic Acidemia
Sponsor: ModernaTX, Inc.
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Propionic Acidemia View
Keywords:

Keywords

Keyword Brief Keyword Text View
None mRNA-3927 View
None Propionic Aciduria View
None Metabolism, Inborn Errors View
None Genetic Diseases View
None Inborn Amino Acid Metabolism, Inborn Errors View
None Acidosis View
None Acid-Base Imbalance View
None Metabolic Diseases View
None Organic Acidemias View
None Moderna View
None mRNA View