Viewing StudyNCT00004386



Ignite Creation Date: 2024-05-05 @ 11:21 AM
Last Modification Date: 2024-10-26 @ 9:04 AM
Study NCT ID: NCT00004386
Status: TERMINATED
Last Update Posted: 2005-06-24
First Post: 1999-10-18

Brief Title: Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency
Sponsor: Eunice Kennedy Shriver National Institute of Child Health and Human Development NICHD
Organization: Office of Rare Diseases ORD

Conditions & Keywords Data

Conditions:
Name
Ornithine Transcarbamylase Deficiency Disease
Keywords:
Name View
urea cycle disorder View
inborn errors of metabolism View
rare disease View