Viewing StudyNCT05788536



Ignite Creation Date: 2024-05-06 @ 6:46 PM
Last Modification Date: 2024-10-26 @ 2:54 PM
Study NCT ID: NCT05788536
Status: RECRUITING
Last Update Posted: 2024-06-21
First Post: 2023-03-15

Brief Title: A Study of DB-OTO an Adeno-associated Virus AAV Based Gene Therapy in ChildrenInfants With Hearing Loss Due to Otoferlin Mutations
Sponsor: Regeneron Pharmaceuticals
Organization: Regeneron Pharmaceuticals

Conditions & Keywords Data

Conditions:
Name
Congenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene OTOF
Keywords:
Name View
DB-OTO View
Gene Therapy View
Congenital Hearing Loss View
Sensorineural Hearing Loss View
Auditory Neuropathy View
Pediatric View
Cochlear Implant View
Otoferlin View
Deaf View
Hard of hearing View
Hearing impaired View
Hearing disorder View
Fully implantable hearing aid View
Child View
Infant View
CHORD View