Viewing StudyNCT05665166



Ignite Creation Date: 2024-05-06 @ 6:26 PM
Last Modification Date: 2024-10-26 @ 2:48 PM
Study NCT ID: NCT05665166
Status: RECRUITING
Last Update Posted: 2023-10-12
First Post: 2022-12-07

Brief Title: Gene Therapy with Modified Autologous Hematopoietic Stem Cells for Patients with Mucopolysaccharidosis Type II
Sponsor: University of Manchester
Organization: University of Manchester

Conditions & Keywords Data

Conditions:
Name
Mucopolysaccharidosis II
Keywords: