Viewing Study NCT04743557


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Study NCT ID: NCT04743557
Status: WITHDRAWN
Last Update Posted: 2022-07-11
First Post: 2021-02-03
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Early Phase Human Drug Trial to Investigate DYN101 in Participants 2 to 17 Years With Centronuclear Myopathies
Sponsor: Dynacure
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Centronuclear Myopathy View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Muscular Diseases View
None Myopathies, Structural, Congenital View
None Musculoskeletal Diseases View
None Neuromuscular Diseases View
None Nervous System Diseases View