Viewing StudyNCT05475691



Ignite Creation Date: 2024-05-06 @ 5:55 PM
Last Modification Date: 2024-10-26 @ 2:38 PM
Study NCT ID: NCT05475691
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-03-08
First Post: 2022-07-19

Brief Title: Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America
Sponsor: Hospital Israelita Albert Einstein
Organization: Hospital Israelita Albert Einstein

Conditions & Keywords Data

Conditions:
Name
Spinal Muscular Atrophy
Keywords:
Name View
Small molecule drug View
Spinal Muscular Atrophy 1 View
Spinal Muscular Atrophy 2 View
Spinal Muscular Atrophy 3 View
Spinal Muscular Atrophy 4 View
SMN1 gene View
Nusinersen View
onasemnogene abeparvovec View