Viewing StudyNCT05477563



Ignite Creation Date: 2024-05-06 @ 5:54 PM
Last Modification Date: 2024-10-26 @ 2:38 PM
Study NCT ID: NCT05477563
Status: RECRUITING
Last Update Posted: 2024-05-16
First Post: 2022-07-26

Brief Title: Evaluation of Efficacy and Safety of a Single Dose of CTX001 in Participants With Transfusion-Dependent β-Thalassemia and Severe Sickle Cell Disease
Sponsor: Vertex Pharmaceuticals Incorporated
Organization: Vertex Pharmaceuticals Incorporated

Conditions & Keywords Data

Conditions:
Name
Beta-Thalassemia
Thalassemia
Hematologic Diseases
Genetic Diseases Inborn
Hemoglobinopathies
Sickle Cell Anemia
Sickle Cell Disease
Keywords: