Viewing StudyNCT05432310



Ignite Creation Date: 2024-05-06 @ 5:48 PM
Last Modification Date: 2024-10-26 @ 2:35 PM
Study NCT ID: NCT05432310
Status: RECRUITING
Last Update Posted: 2024-05-16
First Post: 2022-06-04

Brief Title: Autologous Mobilized Peripheral Blood CD34 Hematopoietic Stem and Progenitor Cells HSPC Transduced With the Elongation Factor Alpha Short Promoter EFS - Adenosine Deaminase ADA Gene EFS-ADA Lentiviral Vector for Adenosine Deaminase Severe Combined Immune Deficiency ADA SCID
Sponsor: University of California Los Angeles
Organization: University of California Los Angeles

Conditions & Keywords Data

Conditions:
Name
Adenosine Deaminase Severe Combined Immune Deficiency
Keywords:
Name View
Reduced Intensity Conditioning with Busulfan View
Gene Therapy View
Hematopoietic Stem Cell View
Lentiviral Vector View