Viewing StudyNCT05438485



Ignite Creation Date: 2024-05-06 @ 5:47 PM
Last Modification Date: 2024-10-26 @ 2:36 PM
Study NCT ID: NCT05438485
Status: TERMINATED
Last Update Posted: 2023-12-27
First Post: 2022-06-27

Brief Title: Natural History Study of Patients With Methylmalonic Acidemia and Propionic Acidemia
Sponsor: HemoShear Therapeutics
Organization: HemoShear Therapeutics

Conditions & Keywords Data

Conditions:
Name
Propionic Acidemia
Methylmalonic Acidemia
Keywords:
Name View
JUMP View
Methylmalonic Acidemia View
Propionic Acidemia View
Organic Acidemia View
Inborn errors of metabolism View
PCCA View
PCCB View
Propionyl-coenzyme A carboxylase View
MMUT View
Methylmalonyl-CoA mutase View
Metabolic disease View
Genetic disease View
HemoShear View
Natural History Study View