Viewing Study NCT03591757


Ignite Creation Date: 2025-12-24 @ 6:44 PM
Ignite Modification Date: 2026-01-15 @ 4:12 AM
Study NCT ID: NCT03591757
Status: COMPLETED
Last Update Posted: 2019-06-14
First Post: 2018-07-09
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Short-term Effects of TOLCAPONE on Transthyretin Stability in Subjects With Leptomeningeal TTR Amyloidosis (ATTR)
Sponsor: Boston University
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Transthyretin Amyloidosis View
None Amyloidosis, Leptomeningeal, Transthyretin-Related View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Tolcapone View
None Transthyretin (TTR) View
None Mutant TTR View
None Plasma TTR View
None CSF TTR View
None Tetramer stability View
None Leptomeningeal View
None Amyloidosis View