Viewing StudyNCT05356195



Ignite Creation Date: 2024-05-06 @ 5:33 PM
Last Modification Date: 2024-10-26 @ 2:31 PM
Study NCT ID: NCT05356195
Status: RECRUITING
Last Update Posted: 2024-06-13
First Post: 2022-04-07

Brief Title: Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Transfusion-Dependent β-Thalassemia TDT
Sponsor: Vertex Pharmaceuticals Incorporated
Organization: Vertex Pharmaceuticals Incorporated

Conditions & Keywords Data

Conditions:
Name
Beta-Thalassemia
Thalassemia
Genetic Diseases Inborn
Hematologic Diseases
Hemoglobinopathies
Keywords: