Viewing StudyNCT05228145



Ignite Creation Date: 2024-05-06 @ 5:10 PM
Last Modification Date: 2024-10-26 @ 2:24 PM
Study NCT ID: NCT05228145
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-09-18
First Post: 2021-12-17

Brief Title: Gene Therapy Study for Children With CLN5 Batten Disease
Sponsor: Neurogene Inc
Organization: Neurogene Inc

Conditions & Keywords Data

Conditions:
Name
Neuronal Ceroid Lipofuscinosis CLN5
Keywords:
Name View
Batten Disease View
Neuronal Ceroid Lipofuscinosis Disease View
Neuronal Ceroid Lipofuscinosis Subtype 5 Disease View
NCL View
Gene Therapy View
Gene Transfer View
CLN5 View
CLN View