Viewing Study NCT03894657


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Study NCT ID: NCT03894657
Status: COMPLETED
Last Update Posted: 2025-08-29
First Post: 2019-02-12
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Validation of Respiratory Epithelial Functional Assessment to Predict Clinical Efficacy of Orkambi®.
Sponsor: Assistance Publique - Hôpitaux de Paris
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Cystic Fibrosis View
None Homozygous F508del Mutation View
Keywords:

Keywords

Keyword Brief Keyword Text View
None CYSTIC FIBROSIS View
None ORKAMBI View