Viewing StudyNCT05073133



Ignite Creation Date: 2024-05-06 @ 4:44 PM
Last Modification Date: 2024-10-26 @ 2:15 PM
Study NCT ID: NCT05073133
Status: COMPLETED
Last Update Posted: 2024-05-31
First Post: 2021-09-20

Brief Title: Safety and Efficacy of Intravenous OAV101 AVXS-101 in Pediatric Patients With Spinal Muscular Atrophy SMA OFELIA
Sponsor: Novartis Pharmaceuticals
Organization: Novartis

Conditions & Keywords Data

Conditions:
Name
Muscular Atrophy Spinal
Keywords:
Name View
loss of muscle strength View
Zolgensma View
OAV101 View
AVXS 101 View
gene therapy View
Muscle atrophy View
SBMA View
spinal and bulbar muscular atrophy View
spinal muscular atrophy View
bulbar muscular atrophy View
muscle function View
myopathy View
muscle wasting View
atrophied muscle View