Viewing Study NCT00528268


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Study NCT ID: NCT00528268
Status: COMPLETED
Last Update Posted: 2025-02-28
First Post: 2007-09-10
Is Gene Therapy: True
Has Adverse Events: True

Brief Title: Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular Atrophy
Sponsor: University of Utah
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Spinal Muscular Atrophy View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Spinal Muscular Atrophy View
None SMA View
None Sodium Phenylbutyrate View