Viewing Study NCT03897361


Ignite Creation Date: 2025-12-24 @ 12:41 PM
Ignite Modification Date: 2026-02-02 @ 3:33 AM
Study NCT ID: NCT03897361
Status: COMPLETED
Last Update Posted: 2025-03-20
First Post: 2019-02-06
Is NOT Gene Therapy: True
Has Adverse Events: False

Brief Title: Stem Cell Gene Therapy for Cystinosis
Sponsor: University of California, San Diego
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Lysosomal Storage Diseases View
None Cystinosis View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Cystinosis View
None Lysosomal Storage Disorders View
None LSD View