Viewing StudyNCT04925960



Ignite Creation Date: 2024-05-06 @ 4:15 PM
Last Modification Date: 2024-10-26 @ 2:06 PM
Study NCT ID: NCT04925960
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-06-03
First Post: 2021-06-08

Brief Title: Oral Epalrestat Therapy in Pediatric Subjects With PMM2-CDG
Sponsor: Maggies Pearl LLC
Organization: Maggies Pearl LLC

Conditions & Keywords Data

Conditions:
Name
Phosphomannomutase II Deficiency
Pmm2-CDG
Phosphomannomutase 2 Deficiency
Phosphomannomutase 2 Congenital Disorder of Glycosylation
Phosphomannomutase II Congenital Disorder of Glycosylation
Keywords: