Viewing Study NCT07197268


Ignite Creation Date: 2025-12-24 @ 5:50 PM
Ignite Modification Date: 2026-02-01 @ 7:46 PM
Study NCT ID: NCT07197268
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2025-09-29
First Post: 2025-07-24
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Personalized Antisense Oligonucleotide Therapy for A Single Participant With ASXL3 Gene Mutation
Sponsor: n-Lorem Foundation
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Bainbridge-Ropers Syndrome View
Keywords: