Viewing Study NCT05959668


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Ignite Modification Date: 2026-01-28 @ 8:54 PM
Study NCT ID: NCT05959668
Status: RECRUITING
Last Update Posted: 2024-08-22
First Post: 2023-05-11
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Development of Health-related Quality of Life Instrument for Patients With Cystinosis
Sponsor: Cystinose Stiftung
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Cystinosis View
Keywords:

Keywords

Keyword Brief Keyword Text View
None Health-related quality of life View
None Cystinosis View
None Patient-reported outcome measure View