Viewing StudyNCT04632953



Ignite Creation Date: 2024-05-06 @ 3:26 PM
Last Modification Date: 2024-10-26 @ 1:49 PM
Study NCT ID: NCT04632953
Status: RECRUITING
Last Update Posted: 2024-06-25
First Post: 2020-11-09

Brief Title: Long-Chain Fatty Acid Oxidation Disorders In-Clinic Disease Monitoring Program
Sponsor: Ultragenyx Pharmaceutical Inc
Organization: Ultragenyx Pharmaceutical Inc

Conditions & Keywords Data

Conditions:
Name
Long-chain Fatty Acid Oxidation Disorders LC-FAOD
Keywords:
Name View
Trifunctional Protein Deficiency View
CACT Deficiency View
Carnitine Acylcarnitine Translocase Deficiency View
CPT1 View
CPT2 View
Carnitine Palmitoyltransferase Deficiencies View
VLCAD View
Very Long Chain Acyl Coa Dehydrogenase Deficiency View
LCHAD Deficiency View
Long-chain 3-hydroxyacyl-CoA Dehydrogenase Deficiency View
TFP Deficiency View