Name |
---|
Mucopolysaccharidosis II |
Hemophilia B |
Mucopolysaccharidosis I |
Name | View |
---|---|
MPS | View |
Mucopolysaccharidosis I | View |
Hurler-Scheie Syndrome | View |
Mucopolysaccharidosis II | View |
Hunter Syndrome | View |
Gene Editing | View |
Gene Therapy | View |
Zinc Finger | View |
SB-318 | View |
SB-913 | View |
SB-FIX | View |
Rare | View |
Genetic | View |
DNA | View |
Sangamo | View |
ZFN | View |
Long Term | View |
Hemophilia B | View |