Viewing StudyNCT00418847



Ignite Creation Date: 2024-05-05 @ 5:14 PM
Last Modification Date: 2024-10-26 @ 9:30 AM
Study NCT ID: NCT00418847
Status: COMPLETED
Last Update Posted: 2016-05-19
First Post: 2007-01-04

Brief Title: Pharmacokinetics and Tolerability of Zavesca Miglustat In Patients With Juvenile GM2 Gangliosidosis
Sponsor: The Hospital for Sick Children
Organization: The Hospital for Sick Children

Conditions & Keywords Data

Conditions:
Name
Gangliosidoses GM2
Keywords:
Name View
Miglustat View
pediatrics View
lysosomal storage diseases View
Gangliosidoses GM2 View
Tay-Sachs disease View
Sandhoff disease View
Infantile GM2-activator deficiency View