Viewing StudyNCT04581785



Ignite Creation Date: 2024-05-06 @ 3:17 PM
Last Modification Date: 2024-10-26 @ 1:46 PM
Study NCT ID: NCT04581785
Status: TERMINATED
Last Update Posted: 2024-02-23
First Post: 2020-10-02

Brief Title: Gene Therapy With hLB-001 in Pediatric Patients With Severe Methylmalonic Acidemia
Sponsor: LogicBio Therapeutics Inc
Organization: Alexion Pharmaceuticals Inc

Conditions & Keywords Data

Conditions:
Name
Methylmalonic Acidemia
Keywords:
Name View
inborn errors of metabolism View
mut0 View
mut- View
mut deficiency View
organic acidemia View
SUNRISE View