Viewing StudyNCT04273243



Ignite Creation Date: 2024-05-06 @ 2:18 PM
Last Modification Date: 2024-10-26 @ 1:28 PM
Study NCT ID: NCT04273243
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-02-06
First Post: 2020-02-14

Brief Title: Long-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer
Sponsor: Amicus Therapeutics
Organization: Amicus Therapeutics

Conditions & Keywords Data

Conditions:
Name
CLN6
Batten Disease
Keywords:
Name View
vLINCL6 View
Neuronal ceroid lipofuscinosis View
NCL View
Gene Transfer View