Viewing Study NCT04247750


Ignite Creation Date: 2025-12-24 @ 5:14 PM
Ignite Modification Date: 2026-01-23 @ 8:44 AM
Study NCT ID: NCT04247750
Status: UNKNOWN
Last Update Posted: 2021-11-12
First Post: 2020-01-08
Is Gene Therapy: True
Has Adverse Events: False

Brief Title: Testing SIROLIMUS in Beta-thalassemia Transfusion Dependent Patients (THALA-RAP)
Sponsor: Università degli Studi di Ferrara
Organization:

Conditions & Keywords Data

Conditions:

Conditions

Condition Brief Condition Text View
None Beta-Thalassemia View
Keywords:

Keywords

Keyword Brief Keyword Text View
None rapamycin View
None erythroid differentiation View
None γ-globin View
None fetal haemoglobin View