Name |
---|
Canavan Disease |
Name | View |
---|---|
Neurodevelopmental diseases | View |
Canavan Disease | View |
AAV | View |
AAV9 | View |
Gene therapy | View |
Aspartoacylase | View |
ASPA | View |
ASPA gene | View |
rAAV9 | View |
ACY2 | View |
Aminoacylase 2 | View |
Spongy degeneration | View |
N-acetyl-L-aspartic acid NAA | View |
N-acetylaspartate | View |
Rare disease | View |
Inherited Metabolic Disorders | View |
Leukodystrophy | View |
Leukoencephalopathies | View |
Autosomal Recessive Disorder | View |