Viewing StudyNCT04126005



Ignite Creation Date: 2024-05-06 @ 1:47 PM
Last Modification Date: 2024-10-26 @ 1:20 PM
Study NCT ID: NCT04126005
Status: RECRUITING
Last Update Posted: 2023-07-12
First Post: 2019-10-10

Brief Title: Natural History Study of Patients With Canavan Disease CANinform Study
Sponsor: Aspa Therapeutics
Organization: Aspa Therapeutics

Conditions & Keywords Data

Conditions:
Name
Canavan Disease
Keywords:
Name View
Neurodevelopmental diseases View
Canavan Disease View
AAV View
AAV9 View
Gene therapy View
Aspartoacylase View
ASPA View
ASPA gene View
rAAV9 View
ACY2 View
Aminoacylase 2 View
Spongy degeneration View
N-acetyl-L-aspartic acid NAA View
N-acetylaspartate View
Rare disease View
Inherited Metabolic Disorders View
Leukodystrophy View
Leukoencephalopathies View
Autosomal Recessive Disorder View