Viewing StudyNCT03913143



Ignite Creation Date: 2024-05-06 @ 1:02 PM
Last Modification Date: 2024-10-26 @ 1:07 PM
Study NCT ID: NCT03913143
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2022-03-17
First Post: 2019-02-21

Brief Title: A Study to Evaluate Efficacy Safety Tolerability and Exposure After a Repeat-dose of Sepofarsen QR-110 in LCA10 ILLUMINATE
Sponsor: ProQR Therapeutics
Organization: ProQR Therapeutics

Conditions & Keywords Data

Conditions:
Name
Retinal Disease
Leber Congenital Amaurosis 10
Blindness
Leber Congenital Amaurosis
Vision Disorders
Sensation Disorders
Neurologic Manifestations
Eye Diseases
Eye Diseases Hereditary
Eye Disorders Congenital
Keywords:
Name View
sepofarsen View
LCA10 View
CEP290 View
pCys998X View
c29911655AG View
Lebers Congenital Amaurosis View
Antisense oligonucleotide View
RNA therapy View
QR-110 View