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Ignite Creation Date:
2024-05-06 @ 1:02 PM
Last Modification Date:
2024-10-26 @ 1:07 PM
Study NCT ID:
NCT03913143
Status:
ACTIVE_NOT_RECRUITING
Last Update Posted:
2022-03-17
First Post:
2019-02-21
Brief Title:
A Study to Evaluate Efficacy Safety Tolerability and Exposure After a Repeat-dose of Sepofarsen QR-110 in LCA10 ILLUMINATE
Sponsor:
ProQR Therapeutics
Organization:
ProQR Therapeutics
Overview
Dates
Organization
Conditions
Design
Enrollment
Locations
Outcomes
Conditions & Keywords Data
Conditions:
Name
Retinal Disease
Leber Congenital Amaurosis 10
Blindness
Leber Congenital Amaurosis
Vision Disorders
Sensation Disorders
Neurologic Manifestations
Eye Diseases
Eye Diseases Hereditary
Eye Disorders Congenital
Keywords:
Name
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sepofarsen
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LCA10
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CEP290
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pCys998X
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c29911655AG
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Lebers Congenital Amaurosis
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Antisense oligonucleotide
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RNA therapy
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QR-110
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