Viewing StudyNCT03872479



Ignite Creation Date: 2024-05-06 @ 12:53 PM
Last Modification Date: 2024-10-26 @ 1:05 PM
Study NCT ID: NCT03872479
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2022-12-05
First Post: 2018-10-12

Brief Title: Single Ascending Dose Study in Participants With LCA10
Sponsor: Editas Medicine Inc
Organization: Editas Medicine Inc

Conditions & Keywords Data

Conditions:
Name
Eye Disorders Congenital
Leber Congenital Amaurosis 10
Inherited Retinal Dystrophies
Eye Diseases Hereditary
Retinal Disease
Retinal Degeneration
Vision Disorders
Keywords:
Name View
Cas9 Enzyme View
CEP290 View
LCA10 View
Retinal degenerative diseases RDD View
Leber congenital amaurosis LCA View
Congenital Retinal Blindness View
pCys998X View
c29911655AG View
CRISPR Treatment View
Cas9 Protein View
Eye Diseases Signs and Symptoms View
Genetic Diseases Inborn View
Congenital Abnormalities View
Eye Abnormalities View
CRISPR-Cas9 View
CRISPR Associated Protein 9 View