Viewing StudyNCT00004498



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Last Modification Date: 2024-10-26 @ 9:04 AM
Study NCT ID: NCT00004498
Status: TERMINATED
Last Update Posted: 2015-03-25
First Post: 1999-10-18

Brief Title: Phase I Study of Adenoviral Vector Mediated Gene Transfer for Ornithine Transcarbamylase in Adults With Partial Ornithine Transcarbamylase Deficiency
Sponsor: University of Pennsylvania
Organization: FDA Office of Orphan Products Development

Conditions & Keywords Data

Conditions:
Name
Ornithine Transcarbamylase Deficiency Disease
Keywords:
Name View
urea cycle disorder View
genetic diseases and dysmorphic syndromes View
inborn errors of metabolism View
ornithine transcarbamylase deficiency View
rare disease View