Viewing StudyNCT03770572



Ignite Creation Date: 2024-05-06 @ 12:30 PM
Last Modification Date: 2024-10-26 @ 12:59 PM
Study NCT ID: NCT03770572
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2023-08-29
First Post: 2018-12-07

Brief Title: Gene Therapy for Children With CLN3 Batten Disease
Sponsor: Amicus Therapeutics
Organization: Amicus Therapeutics

Conditions & Keywords Data

Conditions:
Name
CLN3
Batten Disease
Keywords:
Name View
Gene Transfer View
CLN3 View
Neuronal ceroid lipofuscinosis View
NCL View