Ignite Creation Date:
2025-12-24 @ 4:51 PM
Ignite Modification Date:
2026-02-06 @ 8:33 AM
Study NCT ID:
NCT01963650
Status:
TERMINATED
Last Update Posted:
2021-03-17
First Post:
2013-10-11
Is Gene Therapy:
True
Has Adverse Events:
False
Brief Title:
Natural History Study of Children With Metachromatic Leukodystrophy
Sponsor:
Shire
Organization:
Conditions & Keywords Data
Conditions:
Conditions
| Condition Brief | Condition Text | View |
|---|---|---|
| None | Lipid Metabolism Disorders | View |
| None | Metachromatic Leukodystrophy (MLD) | View |
| None | Nervous System Diseases | View |
| None | Brain Diseases | View |
| None | Central Nervous System Diseases | View |
| None | Demyelinating Diseases | View |
| None | Metabolism, Inborn Errors | View |
| None | Genetic Diseases, Inborn | View |
| None | Sphingolipidoses | View |
| None | Hereditary Central Nervous System Demyelinating Diseases | View |
| None | Metabolic Inborn Brain Diseases | View |
| None | Lysosomal Storage Diseases | View |
| None | Metabolic Diseases | View |
| None | Sulfatidosis | View |
Keywords: