Viewing StudyNCT03655678



Ignite Creation Date: 2024-05-06 @ 12:00 PM
Last Modification Date: 2024-10-26 @ 12:53 PM
Study NCT ID: NCT03655678
Status: ACTIVE_NOT_RECRUITING
Last Update Posted: 2024-05-13
First Post: 2018-08-29

Brief Title: A Safety and Efficacy Study Evaluating CTX001 in Subjects With Transfusion-Dependent β-Thalassemia
Sponsor: Vertex Pharmaceuticals Incorporated
Organization: Vertex Pharmaceuticals Incorporated

Conditions & Keywords Data

Conditions:
Name
Hemoglobinopathies
Beta-Thalassemia
Thalassemia
Genetic Diseases Inborn
Hematologic Diseases
Keywords:
Name View
Hemoglobinopathies View
CRISPR-Cas9 View
Beta-Thalassemia View